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Patient Preferences in Rare Diseases: A Qualitative Study in Neuromuscular Disorders to Inform a Quantitative Preference Study

INTRODUCTION: It has become increasingly important to include patient preference information in decision-making processes for drug development. As neuromuscular disorders represent multisystem, debilitating, and progressive rare diseases with few treatment options, this study aimed to explore unmet...

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Detalles Bibliográficos
Autores principales:	Jimenez-Moreno, A. Cecilia, van Overbeeke, Eline, Pinto, Cathy Anne, Smith, Ian, Sharpe, Jenny, Ormrod, James, Whichello, Chiara, de Bekker-Grob, Esther W., Bullok, Kristin, Levitan, Bennett, Huys, Isabelle, de Wit, G. Ardine, Gorman, Grainne
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Springer International Publishing 2021
Materias:	Original Research Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8357717/ https://www.ncbi.nlm.nih.gov/pubmed/33660162 http://dx.doi.org/10.1007/s40271-020-00482-z

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