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Development of a novel PRO instrument for use in familial chylomicronemia syndrome

BACKGROUND: Familial chylomicronemia syndrome (FCS), a rare genetic disorder characterized by high levels of circulating triglycerides, negatively impacts multiple organs, including the liver and pancreas. OBJECTIVE: The objective of this study was to develop and support the content validity of a no...

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Detalles Bibliográficos
Autores principales:	Davidson, David, Slota, Christina, Vera-Llonch, Montserrat, Brown, T. Michelle, Hsieh, Andrew, Fehnel, Sheri
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Springer International Publishing 2021
Materias:	Research
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8357905/ https://www.ncbi.nlm.nih.gov/pubmed/34382114 http://dx.doi.org/10.1186/s41687-021-00347-5

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