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“Growth patterns in children with mucopolysaccharidosis type I-Hurler after hematopoietic stem cell transplantation: Comparison with untreated patients”

The impact of hematopoietic stem cell transplantation (HSCT) on growth in patients diagnosed with mucopolysaccharidosis I Hurler (MPS-IH) has been historically regarded as unsatisfactory. Nevertheless, the growth patterns recorded in transplanted patients have always been compared to those of health...

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Detalles Bibliográficos
Autores principales:	Cattoni, Alessandro, Chiaraluce, Sofia, Gasperini, Serena, Molinari, Silvia, Biondi, Andrea, Rovelli, Attilio, Parini, Rossella
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Elsevier 2021
Materias:	Research Paper
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8361197/ https://www.ncbi.nlm.nih.gov/pubmed/34408967 http://dx.doi.org/10.1016/j.ymgmr.2021.100787

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