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Cross-Sectional Analysis of Baseline Visual Parameters in Subjects Recruited Into the RESCUE and REVERSE ND4-LHON Gene Therapy Studies
This report presents a cross-sectional analysis of the baseline characteristics of subjects with Leber hereditary optic neuropathy enrolled in the gene therapy trials RESCUE and REVERSE, to illustrate the evolution of visual parameters over the first year after vision loss. METHODS: RESCUE and REVER...
Autores principales: | Moster, Mark L., Sergott, Robert C., Newman, Nancy J., Yu-Wai-Man, Patrick, Carelli, Valerio, Bryan, Molly Scannell, Smits, Gerard, Biousse, Valérie, Vignal-Clermont, Catherine, Klopstock, Thomas, Sadun, Alfredo A., DeBusk, Adam A., Carbonelli, Michele, Hage, Rabih, Priglinger, Siegfried, Karanjia, Rustum, Blouin, Laure, Taiel, Magali, Katz, Barrett, Sahel, José Alain |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Journal of Neuro-Ophthalmology
2021
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8366757/ https://www.ncbi.nlm.nih.gov/pubmed/34310464 http://dx.doi.org/10.1097/WNO.0000000000001316 |
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