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Prompt Agalsidase Alfa Therapy Initiation is Associated with Improved Renal and Cardiovascular Outcomes in a Fabry Outcome Survey Analysis

BACKGROUND: The timing of enzyme replacement therapy initiation in patients with Fabry disease is hypothesized to be critical. In this study, we used Fabry Outcome Survey data to assess the impact of prompt versus delayed initiation of treatment with agalsidase alfa on cardiovascular and renal event...

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Detalles Bibliográficos
Autores principales:	Hughes, Derralynn, Linhart, Aleš, Gurevich, Andrey, Kalampoki, Vasiliki, Jazukeviciene, Dalia, Feriozzi, Sandro
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Dove 2021
Materias:	Original Research
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8379390/ https://www.ncbi.nlm.nih.gov/pubmed/34429585 http://dx.doi.org/10.2147/DDDT.S313789

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