A Canadian Adult Spinal Muscular Atrophy Outcome Measures Toolkit: Results of a National Consensus using a Modified Delphi Method

BACKGROUND: Spinal Muscular Atrophy (SMA) is a rare disease that affects 1 in 11 000 live births. Recent developments in SMA treatments have included new disease-modifying therapies that require high quality data to inform decisions around initiation and continuation of therapy. In Canada, there are...

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Detalles Bibliográficos
Autores principales: Slayter, Jeremy, Hodgkinson, Victoria, Lounsberry, Josh, Brais, Bernard, Chapman, Kristine, Genge, Angela, Izenberg, Aaron, Johnston, Wendy, Lochmüller, Hanns, O’Ferrall, Erin, Pfeffer, Gerald, Plamondon, Stephanie, Rodrigue, Xavier, Schellenberg, Kerri, Shoesmith, Christen, Stables, Christine, Taillon, Monique, Warman-Chardon, Jodi, Korngut, Lawrence, O’Connell, Colleen
Formato: Online Artículo Texto
Lenguaje:English
Publicado: IOS Press 2021
Materias:
Research Report
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8385500/
https://www.ncbi.nlm.nih.gov/pubmed/33867362
http://dx.doi.org/10.3233/JND-200617

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