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Characterization of Adult Patients With SMA Treated in US Hospital Settings: A Natural History Study in the Premier Healthcare Database
BACKGROUND: Spinal muscular atrophy (SMA) is a rare genetic disease characterized by progressive muscular weakness and atrophy resulting from motor neuron degeneration. Limited information is available on disease progression among older SMA patients, particularly adults. OBJECTIVE: This study sought...
Autores principales: | Johnson, Nicole B., Proud, Crystal, Wassel, Christina L., Dreyfus, Jill, Cochrane, Thos, Paradis, Angela D. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
IOS Press
2021
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8385506/ https://www.ncbi.nlm.nih.gov/pubmed/33843692 http://dx.doi.org/10.3233/JND-200624 |
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