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Peripheral blood stem and progenitor cell collection in pediatric candidates for ex vivo gene therapy: a 10-year series
Hematopoietic stem and progenitor cell (HSPC)-based gene therapy (GT) requires the collection of a large number of cells. While bone marrow (BM) is the most common source of HSPCs in pediatric donors, the collection of autologous peripheral blood stem cells (PBSCs) is an attractive alternative for G...
Autores principales: | Canarutto, Daniele, Tucci, Francesca, Gattillo, Salvatore, Zambelli, Matilde, Calbi, Valeria, Gentner, Bernhard, Ferrua, Francesca, Marktel, Sarah, Migliavacca, Maddalena, Barzaghi, Federica, Consiglieri, Giulia, Gallo, Vera, Fumagalli, Francesca, Massariello, Paola, Parisi, Cristina, Viarengo, Gianluca, Albertazzi, Elena, Silvani, Paolo, Milani, Raffaella, Santoleri, Luca, Ciceri, Fabio, Cicalese, Maria Pia, Bernardo, Maria Ester, Aiuti, Alessandro |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
American Society of Gene & Cell Therapy
2021
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8390560/ https://www.ncbi.nlm.nih.gov/pubmed/34485596 http://dx.doi.org/10.1016/j.omtm.2021.05.013 |
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