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Therapy Approaches for Stargardt Disease
Despite being the most prevalent cause of inherited blindness in children, Stargardt disease is yet to achieve the same clinical trial success as has been achieved for other inherited retinal diseases. With an early age of onset and continual progression of disease over the life course of an individ...
Autores principales: | Piotter, Elena, McClements, Michelle E, MacLaren, Robert E |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
MDPI
2021
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8393614/ https://www.ncbi.nlm.nih.gov/pubmed/34439845 http://dx.doi.org/10.3390/biom11081179 |
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