Evaluation of putative CSF biomarkers in paediatric spinal muscular atrophy (SMA) patients before and during treatment with nusinersen

Spinal muscular atrophy (SMA) is a genetic neurodegenerative disorder leading to immobilization and premature death. Currently, three alternative therapeutic options are available. Therefore, biomarkers that might reflect or predict the clinical course of the individual patient with treatment are of...

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Detalles Bibliográficos
Autores principales: Johannsen, Jessika, Weiss, Deike, Daubmann, Anne, Schmitz, Leonie, Denecke, Jonas
Formato: Online Artículo Texto
Lenguaje:English
Publicado: John Wiley and Sons Inc. 2021
Materias:
Original Articles
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8419176/
https://www.ncbi.nlm.nih.gov/pubmed/34312963
http://dx.doi.org/10.1111/jcmm.16802

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8419176/
https://www.ncbi.nlm.nih.gov/pubmed/34312963
http://dx.doi.org/10.1111/jcmm.16802

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