Measuring Meaningful Benefit-Risk Tradeoffs to Promote Patient-Focused Drug Development in Prader-Willi Syndrome: A Discrete-Choice Experiment

Background. Prader-Willi syndrome (PWS) is a rare neurodevelopmental disorder causing quality of life impairments such as insatiable hunger (hyperphagia) and obesity. We explored caregivers’ willingness to assume treatment risk in exchange for reduced hyperphagia according to a PWS-validated observe...

Descripción completa

Detalles Bibliográficos
Autores principales: Tsai, Jui-Hua, Crossnohere, Norah L., Strong, Theresa, Bridges, John F. P.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: SAGE Publications 2021
Materias:
Original Research Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8419554/
https://www.ncbi.nlm.nih.gov/pubmed/34497876
http://dx.doi.org/10.1177/23814683211039457

Ejemplares similares

Ejemplares similares