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Colchicine – an effective treatment for children with a clinical diagnosis of autoinflammatory diseases without pathogenic gene variants

BACKGROUND: Autoinflammatory diseases (AID) are rare chronic conditions with high disease burden, affecting children and adults. Clinically and genetically confirmed, AID can be effectively treated with targeted cytokine inhibition. In contrast, for patients with clinical AID symptoms without pathog...

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Detalles Bibliográficos
Autores principales:	Welzel, Tatjana, Wildermuth, Anna L., Deschner, Norbert, Benseler, Susanne M., Kuemmerle-Deschner, Jasmin B.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BioMed Central 2021
Materias:	Research Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8439030/ https://www.ncbi.nlm.nih.gov/pubmed/34521435 http://dx.doi.org/10.1186/s12969-021-00588-0

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