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Alternative Splicing Role in New Therapies of Spinal Muscular Atrophy

It has been estimated that 80% of the pre-mRNA undergoes alternative splicing, which exponentially increases the flow of biological information in cellular processes and can be an attractive therapeutic target. It is a crucial mechanism to increase genetic diversity. Disturbed alternative splicing i...

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Detalles Bibliográficos
Autores principales:	Lejman, Jan, Zieliński, Grzegorz, Gawda, Piotr, Lejman, Monika
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	MDPI 2021
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8468182/ https://www.ncbi.nlm.nih.gov/pubmed/34573328 http://dx.doi.org/10.3390/genes12091346

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