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State of the Art on Approved Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) Modulators and Triple-Combination Therapy

Cystic fibrosis (CF) is the most common life-limiting inherited disease in Caucasian populations, affecting approximately 80,000 people worldwide. CF is a complex multi-organ monogenic autosomal recessive disorder caused by a mutation in cystic fibrosis transmembrane conductance regulator (CFTR) gen...

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Detalles Bibliográficos
Autores principales:	Meoli, Aniello, Fainardi, Valentina, Deolmi, Michela, Chiopris, Giulia, Marinelli, Francesca, Caminiti, Caterina, Esposito, Susanna, Pisi, Giovanna
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	MDPI 2021
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8471029/ https://www.ncbi.nlm.nih.gov/pubmed/34577628 http://dx.doi.org/10.3390/ph14090928

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