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Nusinersen in spinal muscular atrophy type 1 from neonates to young adult: 1-year data from three Asia-Pacific regions

Detalles Bibliográficos
Autores principales:	Chan, Sophelia Hoi-Shan, Chae, Jong-Hee, Chien, Yin-Hsiu, Ko, Tae-Sung, Lee, Jee Hun, Lee, Yun Jeong, Nam, Sang Ook, Jong, Yuh-Jyh
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BMJ Publishing Group 2021
Materias:	PostScript
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8522455/ https://www.ncbi.nlm.nih.gov/pubmed/33574081 http://dx.doi.org/10.1136/jnnp-2020-324532

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