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Gene therapy for cystic fibrosis: new tools for precision medicine

The discovery of the Cystic fibrosis (CF) gene in 1989 has paved the way for incredible progress in treating the disease such that the mean survival age of individuals living with CF is now ~58 years in Canada. Recent developments in gene targeting tools and new cell and animal models have re-ignite...

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Detalles Bibliográficos
Autores principales:	Lee, Jin-A, Cho, Alex, Huang, Elena N., Xu, Yiming, Quach, Henry, Hu, Jim, Wong, Amy P.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BioMed Central 2021
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8556969/ https://www.ncbi.nlm.nih.gov/pubmed/34717671 http://dx.doi.org/10.1186/s12967-021-03099-4

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