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Correction of oxidative stress enhances enzyme replacement therapy in Pompe disease

Pompe disease is a metabolic myopathy due to acid alpha‐glucosidase deficiency. In addition to glycogen storage, secondary dysregulation of cellular functions, such as autophagy and oxidative stress, contributes to the disease pathophysiology. We have tested whether oxidative stress impacts on enzym...

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Detalles Bibliográficos
Autores principales:	Tarallo, Antonietta, Damiano, Carla, Strollo, Sandra, Minopoli, Nadia, Indrieri, Alessia, Polishchuk, Elena, Zappa, Francesca, Nusco, Edoardo, Fecarotta, Simona, Porto, Caterina, Coletta, Marcella, Iacono, Roberta, Moracci, Marco, Polishchuk, Roman, Medina, Diego Luis, Imbimbo, Paola, Monti, Daria Maria, De Matteis, Maria Antonietta, Parenti, Giancarlo
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	John Wiley and Sons Inc. 2021
Materias:	Articles
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8573602/ https://www.ncbi.nlm.nih.gov/pubmed/34606154 http://dx.doi.org/10.15252/emmm.202114434

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