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CFTR Modulator Therapy and Its Impact on Lung Transplantation in Cystic Fibrosis

Cystic fibrosis (CF) is the most common autosomal recessive disorder in Caucasian people and is caused by mutations in the gene encoding for the CF transmembrane conductance regulator (CFTR) protein. It is a multisystem disorder; however, CF lung disease causes most of its morbidity and mortality. A...

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Detalles Bibliográficos
Autores principales: Benden, Christian, Schwarz, Carsten
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Springer Healthcare 2021
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8589902/
https://www.ncbi.nlm.nih.gov/pubmed/34406641
http://dx.doi.org/10.1007/s41030-021-00170-9