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Natural History of Facioscapulohumeral Dystrophy in Children: A 2-Year Follow-up

BACKGROUND AND OBJECTIVES: Data on the natural history of facioscapulohumeral dystrophy (FSHD) in childhood are limited and critical for improved patient care and clinical trial readiness. Our objective was to describe the disease course of FSHD in children. METHODS: We performed a nationwide, singl...

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Detalles Bibliográficos
Autores principales:	Dijkstra, Jildou N., Goselink, Rianne J.M., van Alfen, Nens, de Groot, Imelda J.M., Pelsma, Maaike, van der Stoep, Nienke, Theelen, Thomas, van Engelen, Baziel G.M., Voermans, Nicol C., Erasmus, Corrie E.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Lippincott Williams & Wilkins 2021
Materias:	Research Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8610619/ https://www.ncbi.nlm.nih.gov/pubmed/34675094 http://dx.doi.org/10.1212/WNL.0000000000012882

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