RNA Targeting in Inherited Neuromuscular Disorders: Novel Therapeutic Strategies to Counteract Mis-Splicing

Neuromuscular disorders represent multifaceted abnormal conditions, with little or no cure, leading to patient deaths from complete muscle wasting and atrophy. Despite strong efforts in the past decades, development of effective treatments is still urgently needed. Advent of next-generation sequenci...

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Detalles Bibliográficos
Autores principales: Verdile, Veronica, Guizzo, Gloria, Ferrante, Gabriele, Paronetto, Maria Paola
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2021
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8616048/
https://www.ncbi.nlm.nih.gov/pubmed/34831073
http://dx.doi.org/10.3390/cells10112850

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8616048/
https://www.ncbi.nlm.nih.gov/pubmed/34831073
http://dx.doi.org/10.3390/cells10112850

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