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Gene therapy for ALS: A review

Amyotrophic lateral sclerosis (ALS) has historically posed unique challenges for gene-therapy-based approaches, due to a paucity of therapeutic targets as well as the difficulty of accessing both the brain and spinal cord. Recent advances in our understanding of disease mechanism and ALS genetics, h...

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Detalles Bibliográficos
Autores principales:	Amado, Defne A., Davidson, Beverly L.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	American Society of Gene & Cell Therapy 2021
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8636154/ https://www.ncbi.nlm.nih.gov/pubmed/33839324 http://dx.doi.org/10.1016/j.ymthe.2021.04.008

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