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Eliciting health state utilities for Aromatic L-amino Acid Decarboxylase (AADC) deficiency: a UK vignette study

PURPOSE: The aim of this study was to generate health state utilities for aromatic L-amino acid decarboxylase (AADC) deficiency, a rare genetic, lifelong neurogenerative condition predominantly manifesting in young infants. METHODS: Participants were presented with health state vignettes. These had...

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Detalles Bibliográficos
Autores principales:	Smith, Adam B., Hanbury, Andria, Buesch, Katharina
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Springer International Publishing 2021
Materias:	Research
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8665907/ https://www.ncbi.nlm.nih.gov/pubmed/34897562 http://dx.doi.org/10.1186/s41687-021-00403-0

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