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Exon-Skipping in Duchenne Muscular Dystrophy
Duchenne muscular dystrophy (DMD) is a devastating, rare disease. While clinically described in the 19(th) century, the genetic foundation of DMD was not discovered until more than 100 years later. This genetic understanding opened the door to the development of genetic treatments for DMD. Over the...
| Autores principales: | , , |
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| Formato: | Online Artículo Texto |
| Lenguaje: | English |
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IOS Press
2021
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| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8673534/ https://www.ncbi.nlm.nih.gov/pubmed/34180420 http://dx.doi.org/10.3233/JND-210682 |