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Efficacy of steroid therapy for Fukuyama congenital muscular dystrophy

Although there is only symptomatic treatment for Fukuyama congenital muscular dystrophy (FCMD), several reports have suggested that steroid therapy could be effective for FCMD; however, no independent intervention studies have been conducted. This study aimed to evaluate the efficacy of steroid ther...

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Detalles Bibliográficos
Autores principales:	Murakami, Terumi, Sato, Takatoshi, Adachi, Michiru, Ishiguro, Kumiko, Shichiji, Minobu, Tachimori, Hisateru, Nagata, Satoru, Ishigaki, Keiko
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Nature Publishing Group UK 2021
Materias:	Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8688455/ https://www.ncbi.nlm.nih.gov/pubmed/34930981 http://dx.doi.org/10.1038/s41598-021-03781-z

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