Pharmacological Profile of Viltolarsen for the Treatment of Duchenne Muscular Dystrophy: A Japanese Experience

Duchenne muscular dystrophy (DMD) is a fatal, X-linked recessive disorder characterized by progressive muscle loss and cardiorespiratory complications. Mutations in the DMD gene that eliminate the production of dystrophin protein are the underlying causes of DMD. Viltolarsen is a drug of phosphorodi...

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Detalles Bibliográficos
Autores principales: Roshmi, Rohini Roy, Yokota, Toshifumi
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Dove 2021
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8688746/
https://www.ncbi.nlm.nih.gov/pubmed/34938127
http://dx.doi.org/10.2147/CPAA.S288842

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8688746/
https://www.ncbi.nlm.nih.gov/pubmed/34938127
http://dx.doi.org/10.2147/CPAA.S288842

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