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Crowd Funding for Orphan Drugs: The Case of Baby Pia
Medical crowdfunding is a relatively new strategy to obtain access to orphan drugs. The case of Baby Pia, a Belgian girl with SMA type 1 for whom in 2018 more than $ 2.1 million was raised to get her treated with Zolgensma(®), illustrates well the potential power of medical crowdfunding. But apart f...
Autor principal: | Pinxten, Wim |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Frontiers Media S.A.
2021
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8712947/ https://www.ncbi.nlm.nih.gov/pubmed/34970148 http://dx.doi.org/10.3389/fphar.2021.787342 |
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