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TCRαβ/CD19 depleted HSCT from an HLA-haploidentical relative to treat children with different nonmalignant disorders

Several nonmalignant disorders (NMDs), either inherited or acquired, can be cured by allogeneic hematopoietic stem cell transplantation (HSCT). Between January 2012 and April 2020, 70 consecutive children affected by primary immunodeficiencies, inherited/acquired bone marrow failure syndromes, red b...

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Detalles Bibliográficos
Autores principales: Merli, Pietro, Pagliara, Daria, Galaverna, Federica, Li Pira, Giuseppina, Andreani, Marco, Leone, Giovanna, Amodio, Donato, Pinto, Rita Maria, Bertaina, Alice, Bertaina, Valentina, Mastronuzzi, Angela, Strocchio, Luisa, Boccieri, Emilia, Pende, Daniela, Falco, Michela, Di Nardo, Matteo, Del Bufalo, Francesca, Algeri, Mattia, Locatelli, Franco
Formato: Online Artículo Texto
Lenguaje:English
Publicado: American Society of Hematology 2022
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8753220/
https://www.ncbi.nlm.nih.gov/pubmed/34592755
http://dx.doi.org/10.1182/bloodadvances.2021005628

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