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P104: BASE EDITING REPAIRS THE HBE MUTATION RESTORING THE PRODUCTION OF NORMAL GLOBIN CHAINS IN SEVERE HBE/β-THALASSEMIA PATIENT HEMATOPOIETIC STEM AND ERYTHROID CELLS

Detalles Bibliográficos
Autores principales:	Badat, M, Hua, P, Mettananda, S, Fisher, C, Roy, N, Rice, S, Roy, A, Higgs, D, Davies, J
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Lippincott Williams & Wilkins 2022
Materias:	Poster Presentations
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8811873/ http://dx.doi.org/10.1097/01.HS9.0000821508.47147.52

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