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The Perspective of DMPK on Recombinant Adeno-Associated Virus-Based Gene Therapy: Past Learning, Current Support, and Future Contribution
Given the recent success of gene therapy modalities and the growing number of cell and gene-based therapies in clinical development across many different therapeutic areas, it is evident that this evolving field holds great promise for the unmet medical needs of patients. The recent approvals of Lux...
Autores principales: | Chen, Nancy, Sun, Kefeng, Chemuturi, Nagendra Venkata, Cho, Hyelim, Xia, Cindy Q. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Springer International Publishing
2022
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8817103/ https://www.ncbi.nlm.nih.gov/pubmed/35102450 http://dx.doi.org/10.1208/s12248-021-00678-7 |
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