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Genetically Modified Cell Transplantation Through Macroencapsulated Spheroids with Scaffolds to Treat Fabry Disease

Cell transplantation is expected to be another strategy to treat lysosomal diseases, having several advantages compared to enzyme replacement therapy, such as continuous enzyme secretion and one-time treatment to cure diseases. However, cell transplantation for lysosomal diseases holds issues to be...

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Detalles Bibliográficos
Autores principales:	Kami, Daisuke, Suzuki, Yosuke, Yamanami, Masashi, Tsukimura, Takahiro, Togawa, Tadayasu, Sakuraba, Hitoshi, Gojo, Satoshi
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	SAGE Publications 2021
Materias:	Original Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8842475/ https://www.ncbi.nlm.nih.gov/pubmed/34931534 http://dx.doi.org/10.1177/09636897211060269

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