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Biomarkers for C9orf7-ALS in Symptomatic and Pre-symptomatic Patients: State-of-the-art in the New Era of Clinical Trials
The development of new possible treatments for C9orf72-related ALS and the possibility of early identification of subjects genetically at risk of developing the disease is creating a critical need for biomarkers to track neurodegeneration that could be used as outcome measures in clinical trials. Cu...
Autores principales: | Querin, Giorgia, Biferi, Maria Grazia, Pradat, Pierre-Francois |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
IOS Press
2022
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8842771/ https://www.ncbi.nlm.nih.gov/pubmed/34864683 http://dx.doi.org/10.3233/JND-210754 |
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