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Therapeutic decisions under uncertainty for spinal muscular atrophy: The DECISIONS-SMA study protocol

BACKGROUND: The therapeutic landscape for spinal muscular atrophy has changed in the last few years, encompassing respiratory/motor function and life expectancy benefits. However, physicians still have the challenge of tailoring individuals’ treatment to therapeutic goals, disease progression, patie...

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Detalles Bibliográficos
Autores principales:	Saposnik, Gustavo, Díaz-Abós, Paola, Sánchez-Menéndez, Victoria, Álvarez, Carmen, Terzaghi, María, Maurino, Jorge, Brañas-Pampillón, María, Málaga, Ignacio
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Public Library of Science 2022
Materias:	Study Protocol
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8846509/ https://www.ncbi.nlm.nih.gov/pubmed/35167619 http://dx.doi.org/10.1371/journal.pone.0264006

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