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Gene Therapy Evidence Generation and Economic Analysis: Pragmatic Considerations to Facilitate Fit-for-Purpose Health Technology Assessment

Gene therapies (GTs) are considered to be a paradigm-shifting class of treatments with the potential to treat previously incurable diseases or those with significant unmet treatment needs. However, considerable challenges remain in their health technology assessment (HTA), mainly stemming from the i...

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Detalles Bibliográficos
Autores principales:	Qiu, Tingting, Pochopien, Michal, Liang, Shuyao, Saal, Gauri, Paterak, Ewelina, Janik, Justyna, Toumi, Mondher
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Frontiers Media S.A. 2022
Materias:	Public Health
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8863657/ https://www.ncbi.nlm.nih.gov/pubmed/35223725 http://dx.doi.org/10.3389/fpubh.2022.773629

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