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Long-Term Metabolic Correction of Phenylketonuria by AAV-Delivered Phenylalanine Amino Lyase
Autores principales: | Tao, Rui, Xiao, Lin, Zhou, Lifang, Zheng, Zhaoyue, Long, Jie, Zhou, Lixing, Tang, Minghai, Dong, Biao, Yao, Shaohua |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
American Society of Gene & Cell Therapy
2022
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8891990/ https://www.ncbi.nlm.nih.gov/pubmed/35284591 http://dx.doi.org/10.1016/j.omtm.2022.02.009 |
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