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Anticipating New Treatments for Cystic Fibrosis: A Global Survey of Researchers

Cystic fibrosis is a life-threatening disease that affects at least 100,000 people worldwide. It is caused by a defect in the cystic fibrosis transmembrane regulator (CFTR) gene and presently, 360 CFTR-causing mutations have been identified. Since the discovery of the CFTR gene, the expectation of d...

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Detalles Bibliográficos
Autores principales:	Cabral, Bernardo, Terlizzi, Vito, Laselva, Onofrio, Conte Filho, Carlos, Mota, Fabio
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	MDPI 2022
Materias:	Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8911007/ https://www.ncbi.nlm.nih.gov/pubmed/35268374 http://dx.doi.org/10.3390/jcm11051283

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