Unmet Therapeutic Needs of Non-Ambulatory Patients with Duchenne Muscular Dystrophy: A Mixed-Method Analysis

OBJECTIVE: Duchenne muscular dystrophy has been a launching pad for patient-focused drug development (PFDD). Yet, PFDD efforts have largely neglected non-ambulatory patients. To support PFDD efforts in this population, we primarily sought to understand the needs of non-ambulatory Duchenne patients a...

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Detalles Bibliográficos
Autores principales: Schuster, Anne L. R., Crossnohere, Norah L., Fischer, Ryan, Furlong, Patricia, Bridges, John F. P.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Springer International Publishing 2022
Materias:
Original Research
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8943787/
https://www.ncbi.nlm.nih.gov/pubmed/35325439
http://dx.doi.org/10.1007/s43441-022-00389-x

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