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CRISPR/Cas-Based Gene Editing Strategies for DOCK8 Immunodeficiency Syndrome

Defects in the DOCK8 gene causes combined immunodeficiency termed DOCK8 immunodeficiency syndrome (DIDS). DIDS previously belonged to the disease category of autosomal recessive hyper IgE syndrome (AR-HIES) but is now classified as a combined immunodeficiency (CID). This genetic disorder induces ear...

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Detalles Bibliográficos
Autores principales: Ravendran, Sujan, Hernández, Sabina Sánchez, König, Saskia, Bak, Rasmus O.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Frontiers Media S.A. 2022
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8969908/
https://www.ncbi.nlm.nih.gov/pubmed/35373187
http://dx.doi.org/10.3389/fgeed.2022.793010

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