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Advances of adeno-associated virus applied in gene therapy to hemophilia from bench work to the clinical use
Hemophilia A and B are diseases caused by a single gene deficiency and are thus suitable for gene therapy. In recent clinical research, adeno-associated virus (AAV) was employed by several teams in the treatment of hemophilia A and B, and the outcomes were encouraging. In this review, we summarized...
| Autores principales: | , , |
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| Formato: | Online Artículo Texto |
| Lenguaje: | English |
| Publicado: |
Wolters Kluwer Health
2019
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| Materias: | |
| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8975051/ https://www.ncbi.nlm.nih.gov/pubmed/35402808 http://dx.doi.org/10.1097/BS9.0000000000000030 |