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Long-term prophylaxis with lanadelumab for HAE: authorization for temporary use in France

BACKGROUND: Hereditary angioedema (HAE) is associated with a heavy burden of illness. OBJECTIVE: To evaluate use of lanadelumab in a French Authorization for Temporary Use (ATU) program. METHODS: ATU requests were made between October 12, 2018, and March 13, 2019; patients were followed through Sept...

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Detalles Bibliográficos
Autores principales:	Fain, Olivier, Du-Thanh, Aurelie, Gobert, Delphine, Launay, David, Inhaber, Neil, Boudjemia, Karima, Aubineau, Magali, Sobel, Alain, Boccon-Gibod, Isabelle, Weiss, Laurence, Bouillet, Laurence
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BioMed Central 2022
Materias:	Research
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8976389/ https://www.ncbi.nlm.nih.gov/pubmed/35365234 http://dx.doi.org/10.1186/s13223-022-00664-4

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