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Clinical applications of retinal gene therapies

Retinal degenerative diseases are a major cause of blindness. Retinal gene therapy is a trail-blazer in the human gene therapy field, leading to the first FDA approved gene therapy product for a human genetic disease. The application of Clustered Regularly Interspaced Short Palindromic Repeat/Cas9 (...

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Detalles Bibliográficos
Autores principales:	Fu, Xin, Huu, Viet Anh Nguyen, Duan, Yaou, Kermany, Daniel S, Valentim, Carolina C S, Zhang, Runze, Zhu, Jie, Zhang, Charlotte L, Sun, Xiaodong, Zhang, Kang
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Oxford University Press 2018
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8982485/ https://www.ncbi.nlm.nih.gov/pubmed/35694125 http://dx.doi.org/10.1093/pcmedi/pby004

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