Cargando…

Handling death as an intercurrent event in time to recovery analysis in COVID-19 treatment clinical trials

In clinical trials with the objective to evaluate the treatment effect on time to recovery, such as investigational trials on therapies for COVID-19 hospitalized patients, the patients may face a mortality risk that competes with the opportunity to recover (e.g., be discharged from the hospital). Th...

Descripción completa

Detalles Bibliográficos
Autores principales: Li, Hong, Gleason, Kevin J., Hu, Yiran, Lovell, Sandra S., Mukhopadhyay, Saurabh, Wang, Li, Huang, Bidan
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Elsevier Inc. 2022
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8986229/
https://www.ncbi.nlm.nih.gov/pubmed/35398251
http://dx.doi.org/10.1016/j.cct.2022.106758
_version_ 1784682503153385472
author Li, Hong
Gleason, Kevin J.
Hu, Yiran
Lovell, Sandra S.
Mukhopadhyay, Saurabh
Wang, Li
Huang, Bidan
author_facet Li, Hong
Gleason, Kevin J.
Hu, Yiran
Lovell, Sandra S.
Mukhopadhyay, Saurabh
Wang, Li
Huang, Bidan
author_sort Li, Hong
collection PubMed
description In clinical trials with the objective to evaluate the treatment effect on time to recovery, such as investigational trials on therapies for COVID-19 hospitalized patients, the patients may face a mortality risk that competes with the opportunity to recover (e.g., be discharged from the hospital). Therefore, an appropriate analytical strategy to account for death is particularly important due to its potential impact on the estimation of the treatment effect. To address this challenge, we conducted a thorough evaluation and comparison of nine survival analysis methods with different strategies to account for death, including standard survival analysis methods with different censoring strategies and competing risk analysis methods. We report results of a comprehensive simulation study that employed design parameters commonly seen in COVID-19 trials and case studies using reconstructed data from a published COVID-19 clinical trial. Our research results demonstrate that, when there is a moderate to large proportion of patients who died before observing their recovery, competing risk analyses and survival analyses with the strategy to censor death at the maximum follow-up timepoint would be able to better detect a treatment effect on recovery than the standard survival analysis that treat death as a non-informative censoring event. The aim of this research is to raise awareness of the importance of handling death appropriately in the time-to-recovery analysis when planning current and future COVID-19 treatment trials.
format Online
Article
Text
id pubmed-8986229
institution National Center for Biotechnology Information
language English
publishDate 2022
publisher Elsevier Inc.
record_format MEDLINE/PubMed
spelling pubmed-89862292022-04-07 Handling death as an intercurrent event in time to recovery analysis in COVID-19 treatment clinical trials Li, Hong Gleason, Kevin J. Hu, Yiran Lovell, Sandra S. Mukhopadhyay, Saurabh Wang, Li Huang, Bidan Contemp Clin Trials Article In clinical trials with the objective to evaluate the treatment effect on time to recovery, such as investigational trials on therapies for COVID-19 hospitalized patients, the patients may face a mortality risk that competes with the opportunity to recover (e.g., be discharged from the hospital). Therefore, an appropriate analytical strategy to account for death is particularly important due to its potential impact on the estimation of the treatment effect. To address this challenge, we conducted a thorough evaluation and comparison of nine survival analysis methods with different strategies to account for death, including standard survival analysis methods with different censoring strategies and competing risk analysis methods. We report results of a comprehensive simulation study that employed design parameters commonly seen in COVID-19 trials and case studies using reconstructed data from a published COVID-19 clinical trial. Our research results demonstrate that, when there is a moderate to large proportion of patients who died before observing their recovery, competing risk analyses and survival analyses with the strategy to censor death at the maximum follow-up timepoint would be able to better detect a treatment effect on recovery than the standard survival analysis that treat death as a non-informative censoring event. The aim of this research is to raise awareness of the importance of handling death appropriately in the time-to-recovery analysis when planning current and future COVID-19 treatment trials. Elsevier Inc. 2022-08 2022-04-06 /pmc/articles/PMC8986229/ /pubmed/35398251 http://dx.doi.org/10.1016/j.cct.2022.106758 Text en © 2022 Elsevier Inc. All rights reserved. Since January 2020 Elsevier has created a COVID-19 resource centre with free information in English and Mandarin on the novel coronavirus COVID-19. The COVID-19 resource centre is hosted on Elsevier Connect, the company's public news and information website. Elsevier hereby grants permission to make all its COVID-19-related research that is available on the COVID-19 resource centre - including this research content - immediately available in PubMed Central and other publicly funded repositories, such as the WHO COVID database with rights for unrestricted research re-use and analyses in any form or by any means with acknowledgement of the original source. These permissions are granted for free by Elsevier for as long as the COVID-19 resource centre remains active.
spellingShingle Article
Li, Hong
Gleason, Kevin J.
Hu, Yiran
Lovell, Sandra S.
Mukhopadhyay, Saurabh
Wang, Li
Huang, Bidan
Handling death as an intercurrent event in time to recovery analysis in COVID-19 treatment clinical trials
title Handling death as an intercurrent event in time to recovery analysis in COVID-19 treatment clinical trials
title_full Handling death as an intercurrent event in time to recovery analysis in COVID-19 treatment clinical trials
title_fullStr Handling death as an intercurrent event in time to recovery analysis in COVID-19 treatment clinical trials
title_full_unstemmed Handling death as an intercurrent event in time to recovery analysis in COVID-19 treatment clinical trials
title_short Handling death as an intercurrent event in time to recovery analysis in COVID-19 treatment clinical trials
title_sort handling death as an intercurrent event in time to recovery analysis in covid-19 treatment clinical trials
topic Article
url https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8986229/
https://www.ncbi.nlm.nih.gov/pubmed/35398251
http://dx.doi.org/10.1016/j.cct.2022.106758
work_keys_str_mv AT lihong handlingdeathasanintercurrenteventintimetorecoveryanalysisincovid19treatmentclinicaltrials
AT gleasonkevinj handlingdeathasanintercurrenteventintimetorecoveryanalysisincovid19treatmentclinicaltrials
AT huyiran handlingdeathasanintercurrenteventintimetorecoveryanalysisincovid19treatmentclinicaltrials
AT lovellsandras handlingdeathasanintercurrenteventintimetorecoveryanalysisincovid19treatmentclinicaltrials
AT mukhopadhyaysaurabh handlingdeathasanintercurrenteventintimetorecoveryanalysisincovid19treatmentclinicaltrials
AT wangli handlingdeathasanintercurrenteventintimetorecoveryanalysisincovid19treatmentclinicaltrials
AT huangbidan handlingdeathasanintercurrenteventintimetorecoveryanalysisincovid19treatmentclinicaltrials