Cargando…
Gene Editing for Inherited Red Blood Cell Diseases
Today gene therapy is a real therapeutic option to address inherited hematological diseases that could be beneficial for thousands of patients worldwide. Currently, gene therapy is used to treat different monogenic hematological pathologies, including several red blood cell diseases such as β-thalas...
Autores principales: | Quintana-Bustamante, Oscar, Fañanas-Baquero, Sara, Dessy-Rodriguez, Mercedes, Ojeda-Pérez, Isabel, Segovia, Jose-Carlos |
---|---|
Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Frontiers Media S.A.
2022
|
Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8995967/ https://www.ncbi.nlm.nih.gov/pubmed/35418876 http://dx.doi.org/10.3389/fphys.2022.848261 |
Ejemplares similares
-
Specific correction of pyruvate kinase deficiency-causing point mutations by CRISPR/Cas9 and single-stranded oligodeoxynucleotides
por: Fañanas-Baquero, Sara, et al.
Publicado: (2023) -
Clinically relevant gene editing in hematopoietic stem cells for the treatment of pyruvate kinase deficiency
por: Fañanas-Baquero, Sara, et al.
Publicado: (2021) -
Gene editing of PKLR gene in human hematopoietic progenitors through 5’ and 3’ UTR modified TALEN mRNA
por: Quintana-Bustamante, Oscar, et al.
Publicado: (2019) -
Natural estrogens enhance the engraftment of human hematopoietic stem and progenitor cells in immunodeficient mice
por: Fañanas-Baquero, Sara, et al.
Publicado: (2020) -
The Red Blood Cells on the Move!
por: Bogdanova, Anna, et al.
Publicado: (2018)