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Catching Them Early: Framework Parameters and Progress for Prenatal and Childhood Application of Advanced Therapies

Advanced therapy medicinal products (ATMPs) are medicines for human use based on genes, cells or tissue engineering. After clear successes in adults, the nascent technology now sees increasing pediatric application. For many still untreatable disorders with pre- or perinatal onset, timely interventi...

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Detalles Bibliográficos
Autores principales:	Lederer, Carsten W., Koniali, Lola, Buerki-Thurnherr, Tina, Papasavva, Panayiota L., La Grutta, Stefania, Licari, Amelia, Staud, Frantisek, Bonifazi, Donato, Kleanthous, Marina
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	MDPI 2022
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9031205/ https://www.ncbi.nlm.nih.gov/pubmed/35456627 http://dx.doi.org/10.3390/pharmaceutics14040793

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