Global Regulatory and Public Health Initiatives to Advance Pediatric Drug Development for Rare Diseases

The literature thoroughly describes the challenges of pediatric drug development for rare diseases. This includes (1) generating interest from sponsors, (2) small numbers of children affected by a particular disease, (3) difficulties with study design, (4) lack of definitive outcome measures and ass...

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Detalles Bibliográficos
Autores principales: Epps, Carla, Bax, Ralph, Croker, Alysha, Green, Dionna, Gropman, Andrea, Klein, Agnes V., Landry, Hannah, Pariser, Anne, Rosenman, Marc, Sakiyama, Michiyo, Sato, Junko, Sen, Kuntal, Stone, Monique, Takeuchi, Fumi, Davis, Jonathan M.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Springer International Publishing 2022
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9040360/
https://www.ncbi.nlm.nih.gov/pubmed/35471559
http://dx.doi.org/10.1007/s43441-022-00409-w

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9040360/
https://www.ncbi.nlm.nih.gov/pubmed/35471559
http://dx.doi.org/10.1007/s43441-022-00409-w

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