Nanoemulsions as Gene Delivery in Mucopolysaccharidosis Type I—A Mini-Review

Mucopolysaccharidosis type I (MPS I) is a rare monogenic disease in which glycosaminoglycans’ abnormal metabolism leads to the storage of heparan sulfate and dermatan sulfate in various tissues. It causes its damage and impairment. Patients with the severe form of MPS I usually do not live up to the...

Descripción completa

Detalles Bibliográficos
Autores principales: Zapolnik, Paweł, Pyrkosz, Antoni
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2022
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9103791/
https://www.ncbi.nlm.nih.gov/pubmed/35563175
http://dx.doi.org/10.3390/ijms23094785

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9103791/
https://www.ncbi.nlm.nih.gov/pubmed/35563175
http://dx.doi.org/10.3390/ijms23094785

Ejemplares similares