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Large1 gene transfer in older myd mice with severe muscular dystrophy restores muscle function and greatly improves survival
Muscular dystrophy is a progressive and ultimately lethal neuromuscular disease. Although gene editing and gene transfer hold great promise as therapies when administered before the onset of severe clinical symptoms, it is unclear whether these strategies can restore muscle function and improve surv...
| Autores principales: | , , , , , , , , , |
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| Formato: | Online Artículo Texto |
| Lenguaje: | English |
| Publicado: |
American Association for the Advancement of Science
2022
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| Materias: | |
| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9132445/ https://www.ncbi.nlm.nih.gov/pubmed/35613260 http://dx.doi.org/10.1126/sciadv.abn0379 |