Cargando…
Investigational curative gene therapy approaches to sickle cell disease
Sickle cell disease (SCD) is an inherited blood condition resulting from abnormal hemoglobin production. It is one of the most common genetic diseases in the world. The clinical manifestations are variable and range from recurrent acute and debilitating painful crises to life-threatening pulmonary,...
Autores principales: | Williams, David A., Esrick, Erica |
---|---|
Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
American Society of Hematology
2021
|
Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9153042/ https://www.ncbi.nlm.nih.gov/pubmed/34905048 http://dx.doi.org/10.1182/bloodadvances.2021005567 |
Ejemplares similares
-
GRNDaD: big data and sickle cell disease
por: Lanzkron, Sophie, et al.
Publicado: (2022) -
Why is AAV FVIII gene therapy not approved by the US Food and Drug Administration yet?
por: Arruda, Valder R.
Publicado: (2021) -
The management of venous thromboembolism in hospitalized patients with COVID-19
por: Spyropoulos, Alex C.
Publicado: (2020) -
COVID-19 coagulopathy vs disseminated intravascular coagulation
por: Levi, Marcel
Publicado: (2020) -
Comorbidities in DLBCL: too "Severe4" CAR-T therapy?
por: Qualls, David, et al.
Publicado: (2023)