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Gene therapy access: Global challenges, opportunities, and views from Brazil, South Africa, and India

Gene and cell therapies for a variety of life-limiting illnesses are under investigation, and a small number of commercial products have successfully obtained regulatory approval. The cost of treatment is high, and clinical studies evaluating safety and efficacy are performed predominately in high-i...

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Autores principales: Cornetta, Kenneth, Bonamino, Martín, Mahlangu, Johnny, Mingozzi, Federico, Rangarajan, Savita, Rao, Jayandharan
Formato: Online Artículo Texto
Lenguaje:English
Publicado: American Society of Gene & Cell Therapy 2022
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9171243/
https://www.ncbi.nlm.nih.gov/pubmed/35390542
http://dx.doi.org/10.1016/j.ymthe.2022.04.002
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author Cornetta, Kenneth
Bonamino, Martín
Mahlangu, Johnny
Mingozzi, Federico
Rangarajan, Savita
Rao, Jayandharan
author_facet Cornetta, Kenneth
Bonamino, Martín
Mahlangu, Johnny
Mingozzi, Federico
Rangarajan, Savita
Rao, Jayandharan
author_sort Cornetta, Kenneth
collection PubMed
description Gene and cell therapies for a variety of life-limiting illnesses are under investigation, and a small number of commercial products have successfully obtained regulatory approval. The cost of treatment is high, and clinical studies evaluating safety and efficacy are performed predominately in high-income countries. We reviewed the current status of gene and cell therapies in low- and middle-income countries and highlighted the need and current barriers to access. The state of product development in Brazil, South Africa, and India is discussed, including lessons learned from American Society of Gene and Cell Therapy (ASGCT)-sponsored virtual symposia in each of these countries.
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spelling pubmed-91712432023-06-01 Gene therapy access: Global challenges, opportunities, and views from Brazil, South Africa, and India Cornetta, Kenneth Bonamino, Martín Mahlangu, Johnny Mingozzi, Federico Rangarajan, Savita Rao, Jayandharan Mol Ther Review Gene and cell therapies for a variety of life-limiting illnesses are under investigation, and a small number of commercial products have successfully obtained regulatory approval. The cost of treatment is high, and clinical studies evaluating safety and efficacy are performed predominately in high-income countries. We reviewed the current status of gene and cell therapies in low- and middle-income countries and highlighted the need and current barriers to access. The state of product development in Brazil, South Africa, and India is discussed, including lessons learned from American Society of Gene and Cell Therapy (ASGCT)-sponsored virtual symposia in each of these countries. American Society of Gene & Cell Therapy 2022-06-01 2022-04-04 /pmc/articles/PMC9171243/ /pubmed/35390542 http://dx.doi.org/10.1016/j.ymthe.2022.04.002 Text en © 2022 The Author(s) https://creativecommons.org/licenses/by-nc-nd/4.0/This is an open access article under the CC BY-NC-ND license (http://creativecommons.org/licenses/by-nc-nd/4.0/).
spellingShingle Review
Cornetta, Kenneth
Bonamino, Martín
Mahlangu, Johnny
Mingozzi, Federico
Rangarajan, Savita
Rao, Jayandharan
Gene therapy access: Global challenges, opportunities, and views from Brazil, South Africa, and India
title Gene therapy access: Global challenges, opportunities, and views from Brazil, South Africa, and India
title_full Gene therapy access: Global challenges, opportunities, and views from Brazil, South Africa, and India
title_fullStr Gene therapy access: Global challenges, opportunities, and views from Brazil, South Africa, and India
title_full_unstemmed Gene therapy access: Global challenges, opportunities, and views from Brazil, South Africa, and India
title_short Gene therapy access: Global challenges, opportunities, and views from Brazil, South Africa, and India
title_sort gene therapy access: global challenges, opportunities, and views from brazil, south africa, and india
topic Review
url https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9171243/
https://www.ncbi.nlm.nih.gov/pubmed/35390542
http://dx.doi.org/10.1016/j.ymthe.2022.04.002
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