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Molecular Signatures of Response to Mecasermin in Children With Rett Syndrome

Rett syndrome (RTT) is a devastating neurodevelopmental disorder without effective treatments. Attempts at developing targetted therapies have been relatively unsuccessful, at least in part, because the genotypical and phenotypical variability of the disorder. Therefore, identification of biomarkers...

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Detalles Bibliográficos
Autores principales:	Shovlin, Stephen, Delepine, Chloe, Swanson, Lindsay, Bach, Snow, Sahin, Mustafa, Sur, Mriganka, Kaufmann, Walter E., Tropea, Daniela
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Frontiers Media S.A. 2022
Materias:	Neuroscience
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9197456/ https://www.ncbi.nlm.nih.gov/pubmed/35712450 http://dx.doi.org/10.3389/fnins.2022.868008

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