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LCAT-trial-24 weeks: Protocol for a clinical study to evaluate the safety of regenerative medicine and gene therapy by the autologous transplantation of human lecithin:cholesterol acyltransferase gene-transduced human pre-adipocytes

BACKGROUNDS: Despite the absolute need for life-long treatment of inherited and genetic diseases, there has been little effort to develop such treatments for most of these conditions due to their rarity. Familial lecithin:cholesterol acyltransferase (LCAT) deficiency is recognized as one such orphan...

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Detalles Bibliográficos
Autores principales:	Kuroda, Masayuki, Hori, Makoto, Maezawa, Yoshiro, Kubota, Yoshitaka, Mitsukawa, Nobuyuki, Shiko, Yuki, Ozawa, Yoshihito, Kawasaki, Yohei, Saito, Yasushi, Hanaoka, Hideki, Yokote, Koutaro
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Elsevier 2022
Materias:	Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9207543/ https://www.ncbi.nlm.nih.gov/pubmed/35734220 http://dx.doi.org/10.1016/j.conctc.2022.100946

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